Dystrophy Association

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SciencePress Release2023-03-22 12:00:00
- In NHP, four monthly doses of 20 mg/kg of PGN-EDO51 resulted in 34.9% exon skipped transcripts in biceps; a 14-fold increase over the 2.5% exon 51 skipped...

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SciencePress Release2023-03-20 11:30:00
- Company Presents Overviews of ACHIEVE and DELIVER Global Clinical Trials with Data Anticipated from Both Studies in the Second Half of 2023 - - FORCE...

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SciencePress Release2023-03-21 11:30:00
- BridgeBio has developed a validated bioassay that directly measures glycosylated DG, which is central to LGMD2I disease, and enables monitoring of...

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SciencePress Release2023-03-22 11:30:00
Achieved clinical validation of PRISM platform in 2022 demonstrated ability to potently and durably engage RNA targets and translate preclinical data to the...

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SciencePress Release2023-03-17 11:30:00
- BridgeBio will also share 15-month Phase 2 data and review the Phase 3 clinical trial design of BBP-418, a potential therapeutic for patients with LGMD2I,...

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Business / FinanceBy Pr Newswire2023-03-22 09:30:00
APDA Connects & Supports the Parkinson's Community in April and Year-Round. With a PD Diagnosis Every 6 Minutes, Awareness is Needed Now More than Ever....

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Suneel Ram Teams up with Zuiker, creator of the world-renowned CSI franchise, to share his story of courage, strength and perseverance to educate young...

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SciencePress Release2023-03-22 12:30:00
Results from survey of Urea Cycle Disorders (UCD) healthcare providers show taste and odor were the most important attributes when considering treatment...

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Business / FinanceBy Globe Newswire2023-03-21 20:30:00
LYON, France, March 21, 2023 -- EDAP TMS SA EDAP ("the Company"), a global leader in robotic energy-based therapies, today announced a recent presentation of...

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Business / FinanceBy Pr Newswire2023-03-22 11:00:00
The awards were presented to Senator Susan Collins, Senator Jeanne Shaheen, and Rep. Diane DeGette during JDRF's annual Government Day on Capitol Hill The...

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Bioidentical hormone therapy is a way to replace imbalanced or improperly functioning hormones in the body, which are vital to overall health ALBUQUERQUE,...

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TechnologyPress Release2023-03-22 11:30:00
– The partnership will harness genetic and clinical data from millions of patients tested at Invitae and Deerfield's expertise in drug discovery to address...

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SciencePress Release2023-03-22 06:00:00
Roche and Lilly will collaborate on the development of Roche Diagnostics Elecsys Amyloid Plasma Panel The Elecsys Amyloid Plasma Panel has demonstrated...

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Business / FinanceBy Business Wire2023-03-22 15:21:00
A JAMA Psychiatry study, led by Jarratt D. Pytell, MD, MHS, Department of Medicine, University of Colorado School of Medicine, and co-authored by Brendan...

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Business / Finance2023-03-22 13:26:21
The Federal Reserve, led by Chairman Jerome Powell, faces a tough balancing act in fighting inflation while also ensuring stability of the financial system....

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HealthPress Release2023-03-22 12:00:00
Agreement with Beth Israel Deaconess Medical Center Solidifies Important Technology for CND's Syn-One Test ® and Creates Opportunity for Future Innovations...

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HealthBy Izzy Hawksworth2023-03-22 14:58:29
A care worker has told how he grew an astonishing 18 inches - after having a brain tumour removed when he was a teenager. Jamie Connolly just thought he was...

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SciencePress Release2023-03-22 12:00:00
BRIDGEWATER, N.J., March 22, 2023 (GLOBE NEWSWIRE) -- VYNE Therapeutics Inc. (Nasdaq: VYNE) (VYNE or the Company), a clinical-stage biopharmaceutical company...

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PoliticsBy Health Day2023-03-22 11:35:00
By Cara Murez HealthDay Reporter WEDNESDAY, March 22, 2023 (HealthDay News) -- Multiple sclerosis (MS) and atherosclerosis both involve an abnormal hardening...

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SciencePress Release2023-03-22 11:00:00
Approval extends Evkeeza to children aged 5 to 11 with homozygous familial hypercholesterolemia (HoFH), an inherited condition characterized by extremely...